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Homepage News Research News

September 13, 2017

New trial for a ‘molecular band-aid’ to help DMD hearts and lungs

Several DMD organizations recently teamed up to fund a Phase 2 clinical trial of a new therapy for Duchenne muscular dystrophy (DMD) – Carmeseal-MD. Carmeseal-MD…

Laura dalle-pazze

Love5

Homepage News News

August 31, 2017

Mom Starts Fund to Find Cure for Duchenne Muscular Dystrophy After Son’s Fatal Diagnosis: ‘There’s No Way I Can Give Up’

People.com When Charley Seckler was 3 years old, everyone seemed to notice his big, strong calves. “People always said, ‘Charley, you’re gonna be a soccer…

Charley's Fund Admin

Love2

Homepage News Tracy's Blog

July 31, 2017

“Let’s just say that my life is a combination of bitter and sweet.”

“Let's just say that my life is a combination of bitter and sweet.” I try not to make a habit of plagiarizing my kids, but…

Tracy Seckler

Love2

Homepage News Research News

July 22, 2017

What’s next for exon skipping, the personalized medicine that produces dystrophin?

The first exon-skipping treatment for DMD was approved last year, but this is no time to rest on our laurels. We're funding the development of…

Laura dalle-pazze

Love4

Stem cells isolated from mouse muscle fibers are grown into myotubes in a culture dish. These structures have muscle fiber-like properties useful for testing drugs like NEIs.

Homepage News Research News

April 28, 2017

What are neutrophil elastase inhibitors, and why do they hold promise for DMD?

Charley's Fund, Duchenne UK, and Joining Jack recently announced a collaborative grant to Dr. Dada Pisconti of the University of Liverpool in England. With this…

Laura dalle-pazze

Love6

Homepage News Research News

March 10, 2017

Promising new data about Electrical Impedance Myography for DMD

Harvard doctor and scientist Seward Rutkove recently published new data about Electrical Impedance Myography, a non-invasive outcome measure for Duchenne muscular dystrophy and other muscle diseases. Charley's…

Laura dalle-pazze

Love2

Homepage News Tracy's Blog

February 17, 2017

Marathon Pharmaceuticals, Come on Down

I love good news just as much as the next person, so I would’ve loved to shout from the rooftops last week when the FDA…

Laura dalle-pazze

Love3

Hall of Fame Homepage News

October 30, 2016

Jenna Fields

Jenna Fields, a 7th grader from Potomac, Maryland, was on bus patrol two years ago when she met Owen, an adorable blonde with Duchenne (see the…

Charley's Fund Admin

Love2

Homepage News News Research News

September 19, 2016

FDA grants accelerated approval to first drug for Duchenne muscular dystrophy

The U.S. Food and Drug Administration today approved Exondys 51 (eteplirsen) injection, the first drug approved to treat patients with Duchenne muscular dystrophy (DMD). Exondys…

Charley's Fund Admin

Love1